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Revolutionary treatment for blindness in children

A revolutionary new gene therapy which restores sight will be provided by the NHS, chief executive Simon Stevens has announced .

Babies born with inherited retinal dystrophies disorder have poor sight which swiftly deteriorates, with most losing their vision completely in childhood. Until now no treatment has been available.

The life-changing treatment for children and adults – voretigene neparvovec – is the first in a new generation of gene therapies that can be directly administered to patients, in this case through an injection.

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